Clinical efficacy of nusinersen sodium in the treatment of children with spinal muscular atrophy
GUO Jin, WU Yun-Hong, ZHANG Lin-Xia, JI Hui-Ru, ZHOU Na, HU Xiao-Yue
CJCP . 2024, (7): 743 -749 .  DOI: 10.7499/j.issn.1008-8830.2401082