
Clinical efficacy of nusinersen sodium in the treatment of children with spinal muscular atrophy
GUO Jin, WU Yun-Hong, ZHANG Lin-Xia, JI Hui-Ru, ZHOU Na, HU Xiao-Yue
Chinese Journal of Contemporary Pediatrics ›› 2024, Vol. 26 ›› Issue (7) : 743-749.
Clinical efficacy of nusinersen sodium in the treatment of children with spinal muscular atrophy
Spinal muscular atrophy / Nusinersen sodium / Efficacy / Safety / Child