中国输血依赖型地中海贫血异基因造血干细胞移植治疗指南(2026年)

中国妇幼保健协会地中海贫血防治专业委员会, 中华医学会儿科学分会血液学组, 全国地中海贫血防治协作网, 《中国当代儿科杂志》编辑委员会

中国当代儿科杂志 ›› 2026, Vol. 28 ›› Issue (4) : 389-401.

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中国当代儿科杂志 ›› 2026, Vol. 28 ›› Issue (4) : 389-401. DOI: 10.7499/j.issn.1008-8830.2510038
标准·方案·指南

中国输血依赖型地中海贫血异基因造血干细胞移植治疗指南(2026年)

作者信息 +

Guideline for allogeneic hematopoietic stem cell transplantation in the treatment of transfusion-dependent thalassemia in China (2026)

Author information +
文章历史 +

摘要

该指南制订工作组对近10年异基因造血干细胞移植(allogeneic hematopoietic stem cell transplantation,allo-HSCT)治疗输血依赖型地中海贫血(transfusion-dependent thalassemia, TDT)相关文献进行全面检索、评价、遴选和整合,针对allo-HSCT治疗TDT相关的10个临床问题,形成26条推荐意见,旨在指导和规范我国allo-HSCT治疗TDT的临床诊疗实践。

Abstract

A comprehensive retrieval, evaluation, selection, and integration of literature on allogeneic hematopoietic stem cell transplantation (allo-HSCT) for transfusion-dependent thalassemia (TDT) published over the past decade was conducted. For 10 clinical questions related to allo-HSCT in TDT, 26 recommendations were developed. The guideline aims to guide and standardize clinical diagnosis and treatment practices of allo-HSCT for TDT in China.

关键词

输血依赖型地中海贫血 / 异基因造血干细胞移植 / 指南

Key words

Transfusion-dependent thalassemia / Allogeneic hematopoietic stem cell transplantation / Guideline

引用本文

导出引用
中国妇幼保健协会地中海贫血防治专业委员会, 中华医学会儿科学分会血液学组, 全国地中海贫血防治协作网, . 中国输血依赖型地中海贫血异基因造血干细胞移植治疗指南(2026年)[J]. 中国当代儿科杂志. 2026, 28(4): 389-401 https://doi.org/10.7499/j.issn.1008-8830.2510038
Committee of Thalassemia Prevention and Treatment, China Maternal and Child Health Association, Subspecialty Group of Hematology, Society of Pediatrics, Chinese Medical Association, China Thalassemia Prevention and Control Collaboration Network, et al. Guideline for allogeneic hematopoietic stem cell transplantation in the treatment of transfusion-dependent thalassemia in China (2026)[J]. Chinese Journal of Contemporary Pediatrics. 2026, 28(4): 389-401 https://doi.org/10.7499/j.issn.1008-8830.2510038

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