Clinical analysis of nusinersen for spinal muscular atrophy types 2 and 3 in children
Hao-Lin DUAN, Ci-Liu ZHANG, Guo-Li WANG, Yi-Wen XU, Tian-Ming WANG, Fang-Yun LIU, Jing PENG
Chinese Journal of Contemporary Pediatrics . 2026, (9): 1070 -1077 .  DOI: 10.7499/j.issn.1008-8830.2601139